This document discusses factors that contribute to the success of clinical trials for rare diseases. It examines which rare diseases had the most clinical trials and how sampling characteristics like gender, age, and location can affect trial success. The document also looks at trends in rare disease clinical trials and which intervention types typically have the shortest time to approval.

1. What Makes Rare
Disease Clinical Trials
Successful?
Temple University Analytics Challenge
Patrick Jurgelewicz, Kevin Hartigan, Matthew Willie

2. Which Rare
Diseases had the
Most Trials?

3. How does
Sampling Affect
Trial Success?
(Gender)

4. How does
Sampling Affect
Trial Success?
(Age)

5. How does
Sampling Affect
Trial Success?
(Location)

6. Can You Identify
Future Trends in
Clinical Trials?

7. Which
intervention types
(drug, biologic,
genetic
behavioral) had
the shortest time
to approval?