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Rare disease
What is Rare disease?
A rare disease is a disease that affects a tiny percentage of the
population. In other words, an orphan disease is a rare disease, which
means that there is a shortage of a market to get support and resources
for discovering treatments for it.
How many people are affected by rare disease?
Most rare diseases are genetic and affect throughout the person's life,
although symptoms do not become immediately visible. There are
various causes of rare diseases. The majority of them are directly caused
a change in genes or chromosomes and are passed from one generation
to the next. Most of the rare diseases appear early in life, and about 30%
of children with these diseases will die after five years of birth. There
may be as many as 7,000 rare diseases. Only a few types of rare diseases
are diagnosed in the United States. The Americans are living with a rare
disease and are estimated at between 25-30 million.
In recent years, rare-disease products have intrigued pharmaceutical and
biotech companies and firms. While the average revenue of a product
from a rare disease may be lower compared with the more traditional
therapeutic areas, but rare diseases are still a lucrative opportunity, and
it has become a target for many companies in today’s competitive rare
disease drug market. As a company commences to analyze the
requirements for successful development and commercialization of a
rare-disease drug, the company will require to be aware of the unique
aspects of the rare disease and how these will take the
commercialization process.
Rare diseases market reports
There is a myriad of pharmaceutical companies that are developing the
drugs for rare diseases like Acute Myeloid Leukemia, Acromegaly, Acute
Respiratory Distress Syndrome, Alopecia Areata, Amyotrophic Lateral
Sclerosis, Anthrax, Pompe disease and many others. One of the leading
companies is DelveInsight that prepares the market reports on rare
diseases. It provides the exhaustive data on Market forecast,
Epidemiology, Market trends, market size, and market analysis covering
the geographical areas like the United States, EU-5 (The United Kingdom,
France, Germany, Italy, and Spain) and Japan. It also proffers
customizable market reports on rare diseases. These rare disease reports
will help many companies in making informed decisions and eventually
help in staying ahead of the competition.

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Rare Disease

  • 1. Rare disease What is Rare disease? A rare disease is a disease that affects a tiny percentage of the population. In other words, an orphan disease is a rare disease, which means that there is a shortage of a market to get support and resources for discovering treatments for it. How many people are affected by rare disease? Most rare diseases are genetic and affect throughout the person's life, although symptoms do not become immediately visible. There are various causes of rare diseases. The majority of them are directly caused a change in genes or chromosomes and are passed from one generation to the next. Most of the rare diseases appear early in life, and about 30% of children with these diseases will die after five years of birth. There may be as many as 7,000 rare diseases. Only a few types of rare diseases are diagnosed in the United States. The Americans are living with a rare disease and are estimated at between 25-30 million. In recent years, rare-disease products have intrigued pharmaceutical and biotech companies and firms. While the average revenue of a product from a rare disease may be lower compared with the more traditional therapeutic areas, but rare diseases are still a lucrative opportunity, and it has become a target for many companies in today’s competitive rare disease drug market. As a company commences to analyze the requirements for successful development and commercialization of a rare-disease drug, the company will require to be aware of the unique aspects of the rare disease and how these will take the commercialization process.
  • 2. Rare diseases market reports There is a myriad of pharmaceutical companies that are developing the drugs for rare diseases like Acute Myeloid Leukemia, Acromegaly, Acute Respiratory Distress Syndrome, Alopecia Areata, Amyotrophic Lateral Sclerosis, Anthrax, Pompe disease and many others. One of the leading companies is DelveInsight that prepares the market reports on rare diseases. It provides the exhaustive data on Market forecast, Epidemiology, Market trends, market size, and market analysis covering the geographical areas like the United States, EU-5 (The United Kingdom, France, Germany, Italy, and Spain) and Japan. It also proffers customizable market reports on rare diseases. These rare disease reports will help many companies in making informed decisions and eventually help in staying ahead of the competition.