The global Pompe disease treatment market size reached US$ 1.0 Billion in 2023. Looking forward, IMARC Group expects the market to reach US$ 1.3 Billion by 2032, exhibiting a growth rate (CAGR) of 2.58% during 2024-2032. More Info:- https://www.imarcgroup.com/pompe-disease-treatment-market

1. Global Pompe Disease
Treatment Market
Research and Forecast
Report 2024-2032
Format: PDF+EXCEL
© 2023 IMARC All Rights Reserved

2. About IMARC Group
International Market Analysis Research and Consulting Group is a leading adviser on management
strategy and market research worldwide. We partner with clients in all regions and industry
verticals to identify their highest-value opportunities, address their most critical challenges, and
transform their businesses.
IMARC’s information products include major market, scientific, economic and technological
developments for business leaders in pharmaceutical, industrial, and high technology
organizations. Market forecasts and industry analysis for biotechnology, advanced materials,
chemicals, food and beverage, travel and tourism, nanotechnology and novel processing methods
are at the top of the company’s expertise.
IMARC’s tailored approach combines unfathomable insight into the dynamics of companies and
markets with close cooperation at all levels of the client organization. This ensures that our clients
achieve unmatchable competitive advantage, build more proficient organizations, and secure lasting
results.

3. Report Highlight
and Description
According to the latest report by IMARC Group, titled "Pompe Disease
Treatment Market: Global Industry Trends, Share, Size, Growth,
Opportunity and Forecast 2024-2032," the global Pompe disease treatment
market size reached US$ 1.0 Billion in 2023.
Factors Affecting the Growth of the Pompe Disease Treatment
Industry:
Government and Regulatory Support:
Strong support from government bodies and regulatory agencies globally
accelerates the growth of the pompe disease treatment industry. These entities
often expedite the approval processes for new therapies and provide funding
for research and development.
Additionally, many countries have implemented newborn screening programs
that include testing for Pompe disease, leading to early treatment initiation
which can significantly improve patient outcomes. Moreover, such policies
encourage pharmaceutical companies to invest in and develop new treatments
and ensure that these innovations reach the market more swiftly, benefiting
patients sooner.

4. Report Highlight
and Description
Increased Awareness and Diagnosis:
Growing awareness of pompe disease among healthcare professionals and the
public leads to earlier and more accurate diagnoses, directly influencing the
demand for treatment solutions. Additionally, educational campaigns and
improved diagnostic tools, such as genetic testing, are identifying more
individuals who can benefit from treatment early in their disease progression.
As awareness increases, so does the engagement of medical communities and
governments in addressing the needs of this patient population, thus further
expanding the growth of the market for pompe disease treatments.
Technological Advancements:
The growth of the Pompe disease treatment industry is primarily influenced by
breakthroughs in biotechnology and genetic engineering. These advancements
have led to the development of more effective enzyme replacement therapies
(ERTs), which are crucial for treating Pompe disease by supplementing the
deficient enzyme in patients.

5. Report Highlight
and Description
Additionally, progress in gene therapy offers the potential for long-term
solutions by addressing the genetic root causes of the disease. Moreover, this
continuous evolution in treatment approaches enhances patient outcomes and
drives industry expansion as new and improved therapies become available to
a broader patient base.
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6. Report Description
Global Pompe Disease Treatment Market Trends:
The global Pompe disease treatment market is witnessing significant growth, primarily driven by the increasing
adoption of enzyme replacement therapies (ERTs), which remain the cornerstone of treatment. There is a growing
emphasis on advancing gene therapy techniques, promising potentially curative benefits, and addressing the
underlying genetic causes of Pompe disease.
Collaborations between pharmaceutical companies and biotech firms are also intensifying, aimed at accelerating
the development and distribution of innovative therapies. Additionally, the market significantly benefits from
enhanced investment in clinical trials to expand the efficacy and application range of existing treatments,
ensuring continual improvements in patient care and outcomes and thus propelling market growth.
Looking forward, IMARC Group expects the market to reach US$ 1.3 Billion by 2032, exhibiting a growth
rate (CAGR) of 2.58% during 2024-2032.
View Report TOC, Figures and Tables: https://www.imarcgroup.com/pompe-disease-treatment-market

7. Report
Segmentation
Treatment Insights:
• Enzyme Replacement Therapy (ERT)
• Substrate Reduction Therapy (SRT)
• Chaperone-Advanced Replacement Therapy
(CART)
• Others
Route of Administration Insights:
• Oral
• Intravenous
• Others
Distribution Channel Insights:
• Hospital and Clinics Pharmacies
• Retail Pharmacies
• Online Pharmacies

8. Report
Segmentation
• Others
Indication Type Insights:
• Infantile-Onset Pompe Disease (IOPD)
• Classic Infantile Form
• Non-Classic Infantile Form
• Late-Onset Pompe Disease (LOPD)
• Others
Regional Insights:
• North America
• Asia-Pacific
• Europe
• Latin America
• Middle East and Africa

9. Competitive
Landscape with
Key Players
• Amicus Therapeutics Inc.
• Audentes Therapeutics Inc. (Astellas US
Holding Inc.)
• Oxyrane UK Limited
• Sanofi S.A.
• Spark Therapeutics Inc

10. Key Questions
Answered in
the Report
How has the global Pompe disease treatment market performed so
far and how will it perform in the coming years?
What are the drivers, restraints, and opportunities in the global
Pompe disease treatment market?
What are the key regional markets?
Which countries represent the most attractive Pompe disease
treatment markets?
What is the breakup of the market based on the treatment?
What is the breakup of the market based on the route of
administration?

11. Key Questions
Answered in
the Report
What is the breakup of the market based on the distribution
channel?
What is the breakup of the market based on the indication type?
What is the competitive structure of the global Pompe disease
treatment market?
Who are the key players/companies in the global Pompe disease
treatment market?

12. Table of
Contents
1 Preface
2 Scope and Methodology
2.1 Objectives of the Study
2.2 Stakeholders
2.3 Data Sources
2.3.1 Primary Sources
2.3.2 Secondary Sources
2.4 Market Estimation
2.4.1 Bottom-Up Approach
2.4.2 Top-Down Approach
2.5 Forecasting Methodology
3 Executive Summary
4 Introduction
4.1 Overview
4.2 Key Industry Trends
5 Global Pompe Disease Treatment Market
5.1 Market Overview
5.2 Market Performance
5.3 Impact of COVID-19
5.4 Market Forecast
6 Market Breakup by Treatment
6.1 Enzyme Replacement Therapy (ERT)
6.1.1 Mark et Trends
6.1.2 Mark et Forecast
6.2 Substrate Reduction Therapy (SRT)
6.2.1 Mark et Trends
6.2.2 Mark et Forecast
6.3 Chaperone-Advanced Replacement Therapy (CART)
6.3.1 Mark et Trends
6.3.2 Mark et Forecast

13. Table of
Contents
6.4 Others
6.4.1 Mark et Trends
6.4.2 Mark et Forecast
7 Market Breakup by Route of Administration
7.1 Oral
7.1.1 Mark et Trends
7.1.2 Mark et Forecast
7.2 Intravenous
7.2.1 Market Trends
7.2.2 Mark et Forecast
7.3 Others
7.3.1 Mark et Trends
7.3.2 Mark et Forecast
8 Market Breakup by Distribution Channel
8.1 Hospital & Clinics Pharmacies
8.1.1 Mark et Trends
8.1.2 Mark et Forecast
8.2 Retail Pharmacies
8.2.1 Mark et Trends
8.2.2 Mark et Forecast
8.3 Online Pharmacies
8.3.1 Mark et Trends
8.3.2 Mark et Forecast
8.4 Others
8.4.1 Mark et Trends
8.4.2 Mark et Forecast
9 Market Breakup by Indication Type
9.1 Infantile-Onset Pompe Disease (IOPD)
9.1.1 Mark et Trends
9.1.2 Mark et Forecast
For more information, visit :
https://www.imarcgroup.com/pompe -disease-treatment-
market/toc

14. Disclaimer
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opinion have been based on information and sources believed to be accurate and reliable at
the time of publishing. International Market Analysis Research and Consulting makes no
representation of warranty of any kind as to the accuracy or completeness of any Information
provided. IMARC accepts no liability whatsoever for any loss or damage resulting from
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